Design of RNAi hairpins for mutation-specific silencing of ataxin-7 and correction of a SCA7 phenotype. (Q33507519)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19789634%20AND%20SRC:MED&resulttype=core&format=json

8 February 2020

title

Design of RNAi hairpins for mutation-specific silencing of ataxin-7 and correction of a SCA7 phenotype (English)

1 reference

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8 February 2020

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8 February 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19789634%20AND%20SRC:MED&resulttype=core&format=json

8 February 2020

1 reference

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8 February 2020

L Jacquie Greenberg

1 reference

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8 February 2020

Patrick B Arbuthnot

series ordinal

1 reference

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8 February 2020

Amr Abdelgany

series ordinal

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8 February 2020

language of work or name

English

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publication date

30 September 2009

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8 February 2020

1 reference

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8 February 2020

volume

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8 February 2020

issue

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8 February 2020

page(s)

e7232

1 reference

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Creative Commons Attribution 4.0 International

8 February 2020

start time

30 September 2009

1 reference

April 2022 Public Data File from Crossref

copyrighted

0 references

cites work

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Determinants of specific RNA interference-mediated silencing of human beta-globin alleles differing by a single nucleotide polymorphism

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21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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A conditional pan-neuronal Drosophila model of spinocerebellar ataxia 7 with a reversible adult phenotype suitable for identifying modifier genes.

21 January 2018

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Loss of wild-type huntingtin influences motor dysfunction and survival in the YAC128 mouse model of Huntington disease

21 January 2018

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RNAi suppresses polyglutamine-induced neurodegeneration in a model of spinocerebellar ataxia.

21 January 2018

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Allele-specific RNAi selectively silences mutant SOD1 and achieves significant therapeutic benefit in vivo.

21 January 2018

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Expression of shRNA from a tissue-specific pol II promoter is an effective and safe RNAi therapeutic

21 January 2018

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On an autosomal dominant form of retinal-cerebellar degeneration: an autopsy study of five patients in one family

21 January 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/19789634

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Loss of endogenous androgen receptor protein accelerates motor neuron degeneration and accentuates androgen insensitivity in a mouse model of X-linked spinal and bulbar muscular atrophy

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/19789634

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Origin of the SCA7 gene mutation in South Africa: implications for molecular diagnostics

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/19789634

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1371/JOURNAL.PONE.0007232

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19789634%20AND%20SRC:MED&resulttype=core&format=json

8 February 2020

0 references

1 reference

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8 February 2020

PubMed publication ID

19789634

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:19789634%20AND%20SRC:MED&resulttype=core&format=json