Pages that link to "Q45880308"

The following pages link to Expanding AAV packaging capacity with trans-splicing or overlapping vectors: a quantitative comparison (Q45880308):

Displaying 50 items.

• Packaging capacity of adeno-associated virus serotypes: impact of larger genomes on infectivity and postentry steps (Q24533013) ‎ (← links)
• Gene therapy: light is finally in the tunnel (Q27000091) ‎ (← links)
• Promising and delivering gene therapies for vision loss (Q27007079) ‎ (← links)
• Gene therapy of inherited retinal degenerations: prospects and challenges (Q27009261) ‎ (← links)
• Advances in gene therapy for muscular dystrophies (Q28073994) ‎ (← links)
• A hybrid vector system expands adeno-associated viral vector packaging capacity in a transgene-independent manner (Q28256353) ‎ (← links)
• Barriers to inhaled gene therapy of obstructive lung diseases: A review (Q29248141) ‎ (← links)
• Generation of novel AAV variants by directed evolution for improved CFTR delivery to human ciliated airway epithelium (Q33482133) ‎ (← links)
• AAV recombineering with single strand oligonucleotides (Q33514824) ‎ (← links)
• Evidence for the failure of adeno-associated virus serotype 5 to package a viral genome > or = 8.2 kb. (Q33730469) ‎ (← links)
• Full-length dystrophin reconstitution with adeno-associated viral vectors (Q33782799) ‎ (← links)
• Gene and cell-mediated therapies for muscular dystrophy. (Q33831193) ‎ (← links)
• Gene therapy for monogenic liver diseases: clinical successes, current challenges and future prospects. (Q33881920) ‎ (← links)
• The potential of adeno-associated viral vectors for gene delivery to muscle tissue (Q33902499) ‎ (← links)
• Efficient production of dual recombinant adeno-associated viral vectors for factor VIII delivery (Q34082003) ‎ (← links)
• Gene therapy of mdx mice with large truncated dystrophins generated by recombination using rAAV6. (Q34473295) ‎ (← links)
• Vector platforms for gene therapy of inherited retinopathies. (Q34561531) ‎ (← links)
• Capsid-expressing DNA in AAV vectors and its elimination by use of an oversize capsid gene for vector production. (Q34770593) ‎ (← links)
• Self-complementary AAV vectors; advances and applications (Q34804660) ‎ (← links)
• High-efficiency promoter-dependent transduction by adeno-associated virus type 6 vectors in mouse lung (Q34845196) ‎ (← links)
• Consequences of DNA-dependent protein kinase catalytic subunit deficiency on recombinant adeno-associated virus genome circularization and heterodimerization in muscle tissue (Q34857785) ‎ (← links)
• Gene therapy progress and prospects: cystic fibrosis (Q34939013) ‎ (← links)
• Promoters and regulatory elements that improve adeno-associated virus transgene expression in the brain (Q34987192) ‎ (← links)
• Barriers to and new approaches for gene therapy and gene delivery in cystic fibrosis. (Q35012413) ‎ (← links)
• Current status of gene therapy for inherited lung diseases (Q35043830) ‎ (← links)
• Natural history of cone disease in the murine model of Leber congenital amaurosis due to CEP290 mutation: determining the timing and expectation of therapy (Q35132187) ‎ (← links)
• Adeno-associated viral vectors. (Q35216648) ‎ (← links)
• Adeno-associated viral vectors for retinal gene transfer. (Q35566831) ‎ (← links)
• Gene Therapy of ABCA4-Associated Diseases (Q35663857) ‎ (← links)
• Novel mini-dystrophin gene dual adeno-associated virus vectors restore neuronal nitric oxide synthase expression at the sarcolemma (Q35678425) ‎ (← links)
• Viral-mediated gene therapy for the muscular dystrophies: successes, limitations and recent advances (Q35847178) ‎ (← links)
• Gene therapy for cystic fibrosis: an example for lung gene therapy (Q35904424) ‎ (← links)
• Recombinant adeno-associated viral (rAAV) vectors as therapeutic tools for Duchenne muscular dystrophy (DMD). (Q35904461) ‎ (← links)
• Identification and Validation of Small Molecules That Enhance Recombinant Adeno-associated Virus Transduction following High-Throughput Screens (Q36009041) ‎ (← links)
• Gene therapy of inherited retinopathies: a long and successful road from viral vectors to patients (Q36147481) ‎ (← links)
• Adeno-associated virus vectors: potential applications for cancer gene therapy (Q36165834) ‎ (← links)
• Hybrid adeno-associated virus bearing nonhomologous inverted terminal repeats enhances dual-vector reconstruction of minigenes in vivo. (Q36238762) ‎ (← links)
• Improved dual AAV vectors with reduced expression of truncated proteins are safe and effective in the retina of a mouse model of Stargardt disease (Q36252017) ‎ (← links)
• Precise hit: adeno-associated virus in gene targeting (Q36302317) ‎ (← links)
• Retinal Gene Therapy: Current Progress and Future Prospects (Q36306263) ‎ (← links)
• Genetic medicines: treatment strategies for hereditary disorders (Q36423907) ‎ (← links)
• Treatment of human disease by adeno-associated viral gene transfer (Q36448393) ‎ (← links)
• Expressing Transgenes That Exceed the Packaging Capacity of Adeno-Associated Virus Capsids (Q36601946) ‎ (← links)
• Gene therapy to create biological pacemakers (Q36626764) ‎ (← links)
• AAV-mediated gene transfer for retinal diseases (Q36708300) ‎ (← links)
• Trans-splicing adeno-associated viral vector-mediated gene therapy is limited by the accumulation of spliced mRNA but not by dual vector coinfection efficiency (Q36728106) ‎ (← links)
• Synthetic intron improves transduction efficiency of trans-splicing adeno-associated viral vectors. (Q36728109) ‎ (← links)
• The use of recombinant adeno-associated virus for skeletal gene therapy (Q36729692) ‎ (← links)
• Progress in gene therapy of dystrophic heart disease (Q36773242) ‎ (← links)
• Retinal gene therapy with a large MYO7A cDNA using adeno-associated virus (Q36808032) ‎ (← links)