Gene therapy progress and prospects: cystic fibrosis (Q34939013)

5 August 2017

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title

Gene therapy progress and prospects: cystic fibrosis. (English)

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5 August 2017

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Griesenbach U

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5 August 2017

Ferrari S

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5 August 2017

Geddes DM

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5 August 2017

Alton EW

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5 August 2017

language of work or name

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1 October 2002

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5 August 2017

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5 August 2017

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5 August 2017

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5 August 2017

page(s)

1344-1350

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Infection of human airway epithelia with H1N1, H2N2, and H3N2 influenza A virus strains

5 August 2017

cites work

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12 December 2020

Targeting transgene expression for cystic fibrosis gene therapy

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12 December 2020

Ca2+-sensitive cytosolic nucleases prevent efficient delivery to the nucleus of injected plasmids.

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12 December 2020

Aerosol and lobar administration of a recombinant adenovirus to individuals with cystic fibrosis. II. Transfection efficiency in airway epithelium

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12 December 2020

Partial correction of endogenous DeltaF508 CFTR in human cystic fibrosis airway epithelia by spliceosome-mediated RNA trans-splicing

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12 December 2020

G-protein-coupled receptors as targets for gene transfer vectors using natural small-molecule ligands

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12 December 2020

Increasing epithelial junction permeability enhances gene transfer to airway epithelia In vivo.

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12 December 2020

Expression of DeltaF508 CFTR in normal mouse lung after site-specific modification of CFTR sequences by SFHR.

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12 December 2020

Endosomal processing limits gene transfer to polarized airway epithelia by adeno-associated virus.

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12 December 2020

Reduced inflammatory response to plasmid DNA vectors by elimination and inhibition of immunostimulatory CpG motifs

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12 December 2020

Repeat administration of DNA/liposomes to the nasal epithelium of patients with cystic fibrosis

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12 December 2020

Adeno-associated virus type 5 (AAV5) but not AAV2 binds to the apical surfaces of airway epithelia and facilitates gene transfer

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12 December 2020

A clinical inflammatory syndrome attributable to aerosolized lipid-DNA administration in cystic fibrosis

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12 December 2020

Inhibition of recombinant adeno-associated virus (rAAV) transduction by bronchial secretions from cystic fibrosis patients

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12 December 2020

Structural alterations of gene complexes by cystic fibrosis sputum

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12 December 2020

Readministration of adenovirus vector in nonhuman primate lungs by blockade of CD40-CD40 ligand interactions

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12 December 2020

Binding of adeno-associated virus type 5 to 2,3-linked sialic acid is required for gene transfer

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12 December 2020

Expanding AAV packaging capacity with trans-splicing or overlapping vectors: a quantitative comparison

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12 December 2020

Multi-organ, multi-lineage engraftment by a single bone marrow-derived stem cell

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12 December 2020

Cystic fibrosis sputum: a barrier to the transport of nanospheres

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12 December 2020

Utilization of synthetic peptides containing nuclear localization signals for nonviral gene transfer systems

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12 December 2020

Filovirus-pseudotyped lentiviral vector can efficiently and stably transduce airway epithelia in vivo

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12 December 2020

Safety and biological efficacy of a lipid-CFTR complex for gene transfer in the nasal epithelium of adult patients with cystic fibrosis

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12 December 2020

The sheep genome contributes to localization of control elements in a human gene with complex regulatory mechanisms

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12 December 2020

Epstein-Barr virus/human vector provides high-level, long-term expression of alpha1-antitrypsin in mice

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12 December 2020

Enhanced epithelial gene transfer by modulation of tight junctions with sodium caprate.

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12 December 2020

Reexpression following readministration of an adenoviral vector in adult mice after initial in utero adenoviral administration

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12 December 2020

Gene transfer into the fetal primate: evidence for the secretion of transgene product

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12 December 2020

Efficient gene transfer to airway epithelium using recombinant Sendai virus.

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12 December 2020

Budesonide enhances repeated gene transfer and expression in the lung with adenoviral vectors

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12 December 2020

A phase I study of aerosolized administration of tgAAVCF to cystic fibrosis subjects with mild lung disease

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12 December 2020

Adenoviral vector expressing ICP47 inhibits adenovirus-specific cytotoxic T lymphocytes in nonhuman primates

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12 December 2020

CFTR with a partially deleted R domain corrects the cystic fibrosis chloride transport defect in human airway epithelia in vitro and in mouse nasal mucosa in vivo

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12 December 2020

Ubiquitination of both adeno-associated virus type 2 and 5 capsid proteins affects the transduction efficiency of recombinant vectors.

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12 December 2020

Transplant immunosuppression increases and prolongs transgene expression following adenoviral-mediated transfection of rat lungs

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12 December 2020

Control of cystic fibrosis transmembrane conductance regulator expression by BAP31.

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12 December 2020

Expression of the human CFTR gene from episomal oriP-EBNA1-YACs in mouse cells

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12 December 2020

Retargeting the coxsackievirus and adenovirus receptor to the apical surface of polarized epithelial cells reveals the glycocalyx as a barrier to adenovirus-mediated gene transfer

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12 December 2020

CFTR modulates lung secretory cell proliferation and differentiation

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12 December 2020

Functional evidence of CFTR gene transfer in nasal epithelium of cystic fibrosis mice in vivo following luminal application of DNA complexes targeted to the serpin-enzyme complex receptor

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12 December 2020

Regulated expression of the human CFTR gene in epithelial cells

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12 December 2020

High and sustained transgene expression in vivo from plasmid vectors containing a hybrid ubiquitin promoter

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12 December 2020

Development of novel formulations that enhance adenoviral-mediated gene expression in the lung in vitro and in vivo.

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12 December 2020

Loss of epithelial integrity resulting from E-cadherin dysfunction predisposes airway epithelial cells to adenoviral infection

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12 December 2020

In utero AAV-mediated gene transfer to rabbit pulmonary epithelium

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12 December 2020

Mucus altering agents as adjuncts for nonviral gene transfer to airway epithelium

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12 December 2020

A novel peptide, THALWHT, for the targeting of human airway epithelia

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12 December 2020

Targeting the urokinase plasminogen activator receptor enhances gene transfer to human airway epithelia.

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12 December 2020

Human coronavirus 229E infects polarized airway epithelia from the apical surface

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12 December 2020

"Stealth" adenoviruses blunt cell-mediated and humoral immune responses against the virus and allow for significant gene expression upon readministration in the lung

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12 December 2020

Perfluorochemical liquid enhances adeno-associated virus-mediated transgene expression in lungs

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12 December 2020

Repeat transduction in the mouse lung by using adeno-associated virus vectors with different serotypes

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12 December 2020

Nuclear translocation of lactosylated poly-L-lysine/cDNA complex in cystic fibrosis airway epithelial cells

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12 December 2020

Increased persistence of lung gene expression using plasmids containing the ubiquitin C or elongation factor 1alpha promoter.

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12 December 2020

EGTA enhancement of adenovirus-mediated gene transfer to mouse tracheal epithelium in vivo

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12 December 2020

Inhibitory effect of cystic fibrosis sputum on adenovirus-mediated gene transfer in cultured epithelial cells

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12 December 2020

Use of perfluorocarbon (fluorinert) to enhance reporter gene expression following intratracheal instillation into the lungs of Balb/c mice: implications for nebulized delivery of plasmids

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12 December 2020

Adenoviral delivery of osteoprotegerin ameliorates bone resorption in a mouse ovariectomy model of osteoporosis

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Crossref

https://api.crossref.org/works/10.1038%2FSJ.GT.3301791

7 January 2021

inferred from DOI database lookup

Identifiers

DOI

10.1038/SJ.GT.3301791

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Dimensions Publication ID

5 August 2017

1028806766

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PMC publication ID

7091818

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