Novel mini-dystrophin gene dual adeno-associated virus vectors restore neuronal nitric oxide synthase expression at the sarcolemma (Q35678425)

9 August 2017

title

Novel mini-dystrophin gene dual adeno-associated virus vectors restore neuronal nitric oxide synthase expression at the sarcolemma (English)

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9 August 2017

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Yadong Zhang

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9 August 2017

Dongsheng Duan

series ordinal

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9 August 2017

publication date

24 October 2011

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9 August 2017

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9 August 2017

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9 August 2017

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9 August 2017

page(s)

98-103

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Duchenne muscular dystrophy gene therapy: Lost in translation?

9 August 2017

cites work

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Efficient transgene reconstitution with hybrid dual AAV vectors carrying the minimized bridging sequences

12 July 2018

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12 July 2018

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Dystrophins carrying spectrin-like repeats 16 and 17 anchor nNOS to the sarcolemma and enhance exercise performance in a mouse model of muscular dystrophy.

12 July 2018

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12 July 2018

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12 July 2018

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12 July 2018

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Microdystrophin gene therapy of cardiomyopathy restores dystrophin-glycoprotein complex and improves sarcolemma integrity in the mdx mouse heart.

12 July 2018

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Nitric oxide contributes to vascular smooth muscle relaxation in contracting fast-twitch muscles

12 July 2018

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12 July 2018

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12 July 2018

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Nitric oxide synthase complexed with dystrophin and absent from skeletal muscle sarcolemma in Duchenne muscular dystrophy

12 July 2018

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Molecular and phenotypic analysis of patients with deletions within the deletion-rich region of the Duchenne muscular dystrophy (DMD) gene

12 July 2018

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The molecular basis for Duchenne versus Becker muscular dystrophy: correlation of severity with type of deletion

12 July 2018

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Very mild muscular dystrophy associated with the deletion of 46% of dystrophin

12 July 2018

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Exploring the molecular basis for variability among patients with Becker muscular dystrophy: dystrophin gene and protein studies

12 July 2018

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A highly functional mini-dystrophin/GFP fusion gene for cell and gene therapy studies of Duchenne muscular dystrophy

12 July 2018

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Modular flexibility of dystrophin: implications for gene therapy of Duchenne muscular dystrophy

25 September 2018

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Expanding AAV packaging capacity with trans-splicing or overlapping vectors: a quantitative comparison

25 September 2018

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Efficient recovery of dysferlin deficiency by dual adeno-associated vector-mediated gene transfer

25 September 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/21933029

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1089/HUM.2011.131

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9 August 2017

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9 August 2017

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