Postnatal genome editing partially restores dystrophin expression in a mouse model of muscular dystrophy. (Q36598414)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26721683%20AND%20SRC:MED&resulttype=core&format=json

3 March 2020

title

Postnatal genome editing partially restores dystrophin expression in a mouse model of muscular dystrophy (English)

1 reference

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3 March 2020

Chengzu Long

1 reference

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3 March 2020

Alex A Mireault

1 reference

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3 March 2020

John R McAnally

1 reference

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3 March 2020

Efrain Sanchez-Ortiz

1 reference

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3 March 2020

Samadrita Bhattacharyya

1 reference

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3 March 2020

John M Shelton

1 reference

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3 March 2020

Rhonda Bassel-Duby

1 reference

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3 March 2020

Eric N Olson

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3 March 2020

language of work or name

English

0 references

publication date

31 December 2015

1 reference

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3 March 2020

1 reference

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3 March 2020

volume

351

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3 March 2020

issue

6271

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3 March 2020

page(s)

400-403

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How much dystrophin is enough: the physiological consequences of different levels of dystrophin in the mdx mouse

3 March 2020

cites work

1 reference

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Gene delivery to the spinal cord using MRI-guided focused ultrasound

9 September 2017

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Multiplex CRISPR/Cas9-based genome editing for correction of dystrophin mutations that cause Duchenne muscular dystrophy.

9 September 2017

1 reference

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CRISPR genome engineering and viral gene delivery: a case of mutual attraction

9 September 2017

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GUIDE-seq enables genome-wide profiling of off-target cleavage by CRISPR-Cas nucleases

9 September 2017

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Genome editing. The new frontier of genome engineering with CRISPR-Cas9

9 September 2017

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Trans-cranial opening of the blood-brain barrier in targeted regions using a stereotaxic brain atlas and focused ultrasound energy

9 September 2017

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Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA

9 September 2017

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Development and applications of CRISPR-Cas9 for genome engineering

9 September 2017

1 reference

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Adeno-associated virus vectors as therapeutic and investigational tools in the cardiovascular system

9 September 2017

1 reference

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Analysis of off-target effects of CRISPR/Cas-derived RNA-guided endonucleases and nickases.

9 September 2017

1 reference

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Cas9 as a versatile tool for engineering biology

9 September 2017

1 reference

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A Programmable Dual-RNA-Guided DNA Endonuclease in Adaptive Bacterial Immunity

9 September 2017

1 reference

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Optimizing exon skipping therapies for DMD.

9 September 2017

1 reference

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Analysis of AAV serotypes 1-9 mediated gene expression and tropism in mice after systemic injection

9 September 2017

1 reference

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Molecular mechanisms of muscular dystrophies: old and new players

9 September 2017

1 reference

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Duchenne muscular dystrophy and dystrophin: pathogenesis and opportunities for treatment

9 September 2017

1 reference

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Advances in Duchenne muscular dystrophy gene therapy

9 September 2017

1 reference

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CRISPR germline engineering--the community speaks

9 September 2017

1 reference

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Unbiased detection of off-target cleavage by CRISPR-Cas9 and TALENs using integrase-defective lentiviral vectors.

30 September 2017

1 reference

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Precise correction of the dystrophin gene in duchenne muscular dystrophy patient induced pluripotent stem cells by TALEN and CRISPR-Cas9.

28 June 2018

1 reference

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CRISPR/Cas9-mediated genome engineering: an adeno-associated viral (AAV) vector toolbox

28 June 2018

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Several rAAV Vectors Efficiently Cross the Blood–brain Barrier and Transduce Neurons and Astrocytes in the Neonatal Mouse Central Nervous System

28 June 2018

1 reference

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Association of dystrophin and an integral membrane glycoprotein.

28 June 2018

1 reference

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Low dystrophin levels in heart can delay heart failure in mdx mice.

28 June 2018

1 reference

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Therapy for Duchenne muscular dystrophy: renewed optimism from genetic approaches

20 September 2018

1 reference

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A single injection of an adeno-associated virus vector into nuclei with divergent connections results in widespread vector distribution in the brain and global correction of a neurogenetic disease

20 September 2018

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Genome engineering using the CRISPR-Cas9 system

20 September 2018

1 reference

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Enhancing translation: guidelines for standard pre-clinical experiments in mdx mice

21 January 2018

1 reference

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Immunohistological intensity measurements as a tool to assess sarcolemma-associated protein expression

21 January 2018

1 reference

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Dystrophin quantification: Biological and translational research implications

21 January 2018

1 reference

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Deficiency of a glycoprotein component of the dystrophin complex in dystrophic muscle

21 January 2018

1 reference

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21 January 2018

Identifiers

DOI

10.1126/SCIENCE.AAD5725

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26721683%20AND%20SRC:MED&resulttype=core&format=json

3 March 2020

1 reference

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3 March 2020

PubMed publication ID

26721683

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:26721683%20AND%20SRC:MED&resulttype=core&format=json