Pages that link to "Q24533013"
The following pages link to Packaging capacity of adeno-associated virus serotypes: impact of larger genomes on infectivity and postentry steps (Q24533013):
Displaying 50 items.
- The therapeutic potential of genome editing for β-thalassemia (Q26766232) (← links)
- Structural Insights into Adeno-Associated Virus Serotype 5 (Q27679454) (← links)
- Mybpc3 gene therapy for neonatal cardiomyopathy enables long-term disease prevention in mice (Q28253008) (← links)
- Adeno-associated virus serotype 9 efficiently targets ischemic skeletal muscle following systemic delivery. (Q30414524) (← links)
- Imaging activity in astrocytes and neurons with genetically encoded calcium indicators following in utero electroporation (Q30640176) (← links)
- Adeno-associated viral vectors and their redirection to cell-type specific receptors (Q30885494) (← links)
- Myosin7a deficiency results in reduced retinal activity which is improved by gene therapy (Q31132177) (← links)
- Designer gene delivery vectors: molecular engineering and evolution of adeno-associated viral vectors for enhanced gene transfer (Q33296224) (← links)
- Characterization of genome integrity for oversized recombinant AAV vector (Q33576852) (← links)
- Limitations of encapsidation of recombinant self-complementary adeno-associated viral genomes in different serotype capsids and their quantitation (Q33586309) (← links)
- Effect of genome size on AAV vector packaging (Q33730405) (← links)
- Evidence for the failure of adeno-associated virus serotype 5 to package a viral genome > or = 8.2 kb. (Q33730469) (← links)
- Optimized adeno-associated virus (AAV)-protein phosphatase-5 helper viruses for efficient liver transduction by single-stranded AAV vectors: therapeutic expression of factor IX at reduced vector doses (Q33832799) (← links)
- Viral vectors for neurotrophic factor delivery: a gene therapy approach for neurodegenerative diseases of the CNS (Q33894621) (← links)
- The potential of adeno-associated viral vectors for gene delivery to muscle tissue (Q33902499) (← links)
- Gene delivery with viral vectors for cerebrovascular diseases (Q33917592) (← links)
- Impact of ETIF deletion on safety and immunogenicity of equine herpesvirus type 1-vectored vaccines (Q34296144) (← links)
- Modular dispensability of dysferlin C2 domains reveals rational design for mini-dysferlin molecules (Q34318021) (← links)
- Proteasome inhibitors enhance gene delivery by AAV virus vectors expressing large genomes in hemophilia mouse and dog models: a strategy for broad clinical application (Q34343763) (← links)
- Efficient transgene reconstitution with hybrid dual AAV vectors carrying the minimized bridging sequences (Q34511733) (← links)
- Vector platforms for gene therapy of inherited retinopathies. (Q34561531) (← links)
- Cystic fibrosis transmembrane conductance regulator with a shortened R domain rescues the intestinal phenotype of CFTR-/- mice. (Q34582621) (← links)
- Lentiviral gene replacement therapy of retinas in a mouse model for Usher syndrome type 1B. (Q34608354) (← links)
- Efficacy and safety of long-term prophylaxis in severe hemophilia A dogs following liver gene therapy using AAV vectors (Q34621668) (← links)
- Self-complementary AAV vectors; advances and applications (Q34804660) (← links)
- A simple method to increase the transduction efficiency of single-stranded adeno-associated virus vectors in vitro and in vivo. (Q34843762) (← links)
- Subretinal gene delivery using helper-dependent adenoviral vectors. (Q35073956) (← links)
- Recombinant AAV-directed gene therapy for type I glycogen storage diseases (Q35078590) (← links)
- Bioengineered coagulation factor VIII enables long-term correction of murine hemophilia A following liver-directed adeno-associated viral vector delivery (Q35184180) (← links)
- Gene Therapy of ABCA4-Associated Diseases (Q35663857) (← links)
- Gene Therapy for the Retinal Degeneration of Usher Syndrome Caused by Mutations in MYO7A (Q35664199) (← links)
- Large-scale production of lentiviral vector in a closed system hollow fiber bioreactor (Q35751032) (← links)
- Targeted genetic manipulations of neuronal subtypes using promoter-specific combinatorial AAVs in wild-type animals (Q35808747) (← links)
- Identification and Validation of Small Molecules That Enhance Recombinant Adeno-associated Virus Transduction following High-Throughput Screens (Q36009041) (← links)
- In vivo gene transfer strategies to achieve partial correction of von Willebrand disease. (Q36084450) (← links)
- Dysferlin and animal models for dysferlinopathy (Q36085192) (← links)
- cis effects in adeno-associated virus type 2 replication (Q36098985) (← links)
- Gene therapy of inherited retinopathies: a long and successful road from viral vectors to patients (Q36147481) (← links)
- Novel Mutant AAV2 Rep Proteins Support AAV2 Replication without Blocking HSV-1 Helpervirus Replication (Q36261377) (← links)
- Retinal Gene Therapy: Current Progress and Future Prospects (Q36306263) (← links)
- Gene therapy strategies for Duchenne muscular dystrophy utilizing recombinant adeno-associated virus vectors. (Q36345325) (← links)
- Serotype-dependent packaging of large genes in adeno-associated viral vectors results in effective gene delivery in mice. (Q36545533) (← links)
- In vitro analysis of promoter activity in Müller cells (Q36580252) (← links)
- The impact of minimally oversized adeno-associated viral vectors encoding human factor VIII on vector potency in vivo (Q36613086) (← links)
- The anti-inflammatory glycoprotein, CD200, restores neurogenesis and enhances amyloid phagocytosis in a mouse model of Alzheimer's disease (Q36635842) (← links)
- AAV-mediated gene transfer for retinal diseases (Q36708300) (← links)
- Synthetic intron improves transduction efficiency of trans-splicing adeno-associated viral vectors. (Q36728109) (← links)
- Production and characterization of adeno-associated viral vectors (Q36779416) (← links)
- Retinal gene therapy with a large MYO7A cDNA using adeno-associated virus (Q36808032) (← links)
- Progress and problems when considering gene therapy for GSD-II. (Q36960374) (← links)