Pages that link to "Q36147481"
The following pages link to Gene therapy of inherited retinopathies: a long and successful road from viral vectors to patients (Q36147481):
Displaying 25 items.
- Genetic manipulation for inherited neurodegenerative diseases: myth or reality? (Q26752831) (← links)
- Review: the history and role of naturally occurring mouse models with Pde6b mutations (Q28304672) (← links)
- BDNF gene therapy induces auditory nerve survival and fiber sprouting in deaf Pou4f3 mutant mice (Q30460999) (← links)
- Successful gene therapy in the RPGRIP1-deficient dog: a large model of cone-rod dystrophy (Q30571313) (← links)
- Mechanisms of blindness: animal models provide insight into distinct CRX-associated retinopathies (Q34254397) (← links)
- Vector platforms for gene therapy of inherited retinopathies. (Q34561531) (← links)
- Recombinant vectors based on porcine adeno-associated viral serotypes transduce the murine and pig retina (Q34631983) (← links)
- Gene Therapy of ABCA4-Associated Diseases (Q35663857) (← links)
- Improvement in vision: a new goal for treatment of hereditary retinal degenerations (Q35805426) (← links)
- Human Adult Retinal Pigment Epithelial Stem Cell-Derived RPE Monolayers Exhibit Key Physiological Characteristics of Native Tissue (Q36267888) (← links)
- Current Challenges and Future Directions in Recombinant AAV-Mediated Gene Therapy of Duchenne Muscular Dystrophy (Q37277411) (← links)
- AAV2/8 vectors purified from culture medium with a simple and rapid protocol transduce murine liver, muscle, and retina efficiently (Q37406911) (← links)
- Effect of bortezomib on the efficacy of AAV9.SERCA2a treatment to preserve cardiac function in a rat pressure-overload model of heart failure. (Q37685861) (← links)
- Beyond traditional pharmacology: new tools and approaches (Q38311702) (← links)
- Localizing the RPGR protein along the cilium: a new method to determine efficacies to treat RPGR mutations (Q38915580) (← links)
- A novel formulation based on 2,3-di(tetradecyloxy)propan-1-amine cationic lipid combined with polysorbate 80 for efficient gene delivery to the retina. (Q39032036) (← links)
- Evaluation of tolerance to lentiviral LV-RPE65 gene therapy vector after subretinal delivery in nonhuman primates. (Q40103624) (← links)
- Gene therapy as a treatment concept for inherited retinal diseases (Q41465719) (← links)
- Delivery of Adeno-Associated Viral Vectors in Adult Mammalian Inner Ear Cell Subtypes without Auditory Dysfunction. (Q45874366) (← links)
- Dual AAV Vectors for Stargardt Disease (Q45875203) (← links)
- Eating my hat? (Q46707941) (← links)
- Synthetic adeno-associated viral vector efficiently targets mouse and non-human primate retina in vivo. (Q47555045) (← links)
- High-throughput screening identifies kinase inhibitors that increase dual AAV vectors transduction <i>in vitro</i> and in mouse retina. (Q54981136) (← links)
- Genetic Mutation Profiles in Korean Patients with Inherited Retinal Diseases. (Q64892421) (← links)
- Microglia in Retinal Degeneration (Q93088329) (← links)