Long-term correction of glycogen storage disease type II with a hybrid Ad-AAV vector (Q40669141)

22 September 2017

title

Long-term correction of glycogen storage disease type II with a hybrid Ad-AAV vector (English)

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22 September 2017

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glycogen storage disease

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Bao-dong Sun

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22 September 2017

Y-T Chen

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22 September 2017

Andrew Bird

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22 September 2017

Andrea Amalfitano

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22 September 2017

Dwight D Koeberl

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22 September 2017

publication date

1 February 2003

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22 September 2017

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22 September 2017

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22 September 2017

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22 September 2017

page(s)

193-201

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Targeted disruption of the acid alpha-glucosidase gene in mice causes an illness with critical features of both infantile and adult human glycogen storage disease type II

22 September 2017

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Systemic correction of the muscle disorder glycogen storage disease type II after hepatic targeting of a modified adenovirus vector encoding human acid-alpha-glucosidase

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Identifiers

DOI

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22 September 2017

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