Molecular signatures of disease brain endothelia provide new sites for CNS-directed enzyme therapy (Q33502598)

27 July 2017

title

Molecular signatures of disease brain endothelia provide new sites for CNS-directed enzyme therapy (English)

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27 July 2017

Yong Hong Chen

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27 July 2017

Michael Chang

series ordinal

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27 July 2017

Beverly L Davidson

series ordinal

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27 July 2017

language of work or name

English

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publication date

13 September 2009

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27 July 2017

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27 July 2017

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27 July 2017

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27 July 2017

page(s)

1215-1218

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In vitro and in vivo gene therapy vector evolution via multispecies interbreeding and retargeting of adeno-associated viruses

27 July 2017

cites work

1 reference

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Construction of diverse adeno-associated viral libraries for directed evolution of enhanced gene delivery vehicles

21 June 2018

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Heparan sulfate proteoglycan binding properties of adeno-associated virus retargeting mutants and consequences for their in vivo tropism

21 June 2018

1 reference

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Directed evolution of adeno-associated virus yields enhanced gene delivery vectors

21 June 2018

1 reference

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Vascular bed-targeted in vivo gene delivery using tropism-modified adeno-associated viruses

21 June 2018

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A mouse model of classical late-infantile neuronal ceroid lipofuscinosis based on targeted disruption of the CLN2 gene results in a loss of tripeptidyl-peptidase I activity and progressive neurodegeneration

21 June 2018

1 reference

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Culture of murine brain microvascular endothelial cells that maintain expression and cytoskeletal association of tight junction-associated proteins

21 June 2018

1 reference

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Random peptide libraries displayed on adeno-associated virus to select for targeted gene therapy vectors

21 June 2018

1 reference

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Incorporation of tumor-targeting peptides into recombinant adeno-associated virus capsids

21 June 2018

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Intraventricular enzyme replacement improves disease phenotypes in a mouse model of late infantile neuronal ceroid lipofuscinosis

21 June 2018

1 reference

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Functional correction of CNS phenotypes in a lysosomal storage disease model using adeno-associated virus type 4 vectors.

31 October 2018

1 reference

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A novel model of murine mucopolysaccharidosis type VII due to an intracisternal a particle element transposition into the beta-glucuronidase gene: clinical and pathologic findings.

31 October 2018

1 reference

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31 October 2018

Identifiers

DOI

10.1038/NM.2025

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Dimensions Publication ID

27 July 2017

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27 July 2017

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