Correction of brain oligodendrocytes by AAVrh.10 intracerebral gene therapy in metachromatic leukodystrophy mice. (Q36147497)

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2 February 2020

title

Correction of brain oligodendrocytes by AAVrh.10 intracerebral gene therapy in metachromatic leukodystrophy mice (English)

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2 February 2020

0 references

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metachromatic leukodystrophy

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2 February 2020

Nathalie Cartier

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2 February 2020

Françoise Piguet

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2 February 2020

Dolan Sondhi

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2 February 2020

Monique Piraud

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2 February 2020

Françoise Fouquet

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2 February 2020

Neil R Hackett

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2 February 2020

Ornella Ahouansou

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2 February 2020

Marie-Thérèse Vanier

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2 February 2020

Patrick Aubourg

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2 February 2020

Ronald G Crystal

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2 February 2020

Caroline Sevin

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publication date

23 July 2012

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2 February 2020

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volume

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issue

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2 February 2020

page(s)

903-914

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Widespread cortical expression of MANF by AAV serotype 7: localization and protection against ischemic brain injury

2 February 2020

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2 October 2017

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Gene therapy of metachromatic leukodystrophy reverses neurological damage and deficits in mice

2 October 2017

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Expression and purification of a human, soluble Arylsulfatase A for Metachromatic Leukodystrophy enzyme replacement therapy

2 October 2017

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2 October 2017

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2 October 2017

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Phenotype of arylsulfatase A-deficient mice: relationship to human metachromatic leukodystrophy

2 October 2017

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Survival advantage of neonatal CNS gene transfer for late infantile neuronal ceroid lipofuscinosis

2 October 2017

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Oligodendrocyte-specific gene expression in mouse brain: use of a myelin-forming cell type-specific promoter in an adeno-associated virus

2 July 2018

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23 September 2018

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23 September 2018

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23 September 2018

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23 September 2018

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23 September 2018

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23 September 2018

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23 September 2018

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23 September 2018

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23 September 2018

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23 September 2018

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23 September 2018

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23 September 2018

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23 September 2018

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12 December 2020

Efficient retrograde neuronal transduction utilizing self-complementary AAV1

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12 December 2020

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12 December 2020

A pedigree study of metachromatic leukodystrophy. Biochemical identification of the carrier state

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12 December 2020

Identifiers

DOI

10.1089/HUM.2012.015

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:22642214%20AND%20SRC:MED&resulttype=core&format=json

2 February 2020

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2 February 2020

PubMed publication ID

22642214

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