(Q36709988)

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Adult bone marrow stem cells for cell and gene therapies: implications for greater use.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Gene therapy for inborn and acquired immune deficiency disorders

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Hematopoietic stem cell transduction by recombinant adeno-associated virus vectors: problems and solutions

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Site-specific genomic integration produces therapeutic Factor IX levels in mice

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Awakening gene therapy with Sleeping Beauty transposons

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Highly efficient endogenous human gene correction using designed zinc-finger nucleases

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

RETRACTED: Complete and persistent phenotypic correction of phenylketonuria in mice by site-specific genome integration of murine phenylalanine hydroxylase cDNA.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

American Society of Gene Therapy (ASGT) ad hoc subcommittee on retroviral-mediated gene transfer to hematopoietic stem cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

HIV, but not murine leukemia virus, vectors mediate high efficiency gene transfer into freshly isolated G0/G1 human hematopoietic stem cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Transduction of human CD34+ cells that mediate long-term engraftment of NOD/SCID mice by HIV vectors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Stable transduction of quiescent CD34(+)CD38(-) human hematopoietic cells by HIV-1-based lentiviral vectors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Therapeutic haemoglobin synthesis in beta-thalassaemic mice expressing lentivirus-encoded human beta-globin

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Gene transfer into murine hematopoietic stem cells with helper-free foamy virus vectors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Foamy virus vector integration sites in normal human cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Quantitative assay for totipotent reconstituting hematopoietic stem cells by a competitive repopulation strategy

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Hematopoietic stem cells engraft in mice with absolute efficiency

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

The relative quiescence of hematopoietic stem cells in nonhuman primates

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

In vivo proliferation and cell cycle kinetics of long-term self-renewing hematopoietic stem cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Behavior of hematopoietic stem cells in a large animal

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Telomere fluorescence measurements in granulocytes and T lymphocyte subsets point to a high turnover of hematopoietic stem cells and memory T cells in early childhood.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Passage through mitosis is required for oncoretroviruses but not for the human immunodeficiency virus

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Progression to the G1b phase of the cell cycle is required for completion of human immunodeficiency virus type 1 reverse transcription in T cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

A nuclear localization signal within HIV-1 matrix protein that governs infection of non-dividing cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

HIV-1 infection of nondividing cells: C-terminal tyrosine phosphorylation of the viral matrix protein is a key regulator

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

The Vpr protein of human immunodeficiency virus type 1 influences nuclear localization of viral nucleic acids in nondividing host cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Viral protein R regulates docking of the HIV-1 preintegration complex to the nuclear pore complex

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

HIV-1 infection of nondividing cells through the recognition of integrase by the importin/karyopherin pathway

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Intracellular trafficking of retroviral genomes during the early phase of infection: viral exploitation of cellular pathways

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Multiply attenuated lentiviral vector achieves efficient gene delivery in vivo

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Gene transfer by lentiviral vectors is limited by nuclear translocation and rescued by HIV-1 pol sequences

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

HIV-1 genome nuclear import is mediated by a central DNA flap

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

The cell cycle independence of HIV infections is not determined by known karyophilic viral elements

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Human cord blood CD34+CD38- cell transduction via lentivirus-based gene transfer vectors.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Transduction of Human CD34+CD38- Bone Marrow and Cord Blood-Derived SCID-Repopulating Cells with Third-Generation Lentiviral Vectors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Nonproductive human immunodeficiency virus type 1 infection in nucleoside-treated G0 lymphocytes

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

HIV-1 entry into quiescent primary lymphocytes: molecular analysis reveals a labile, latent viral structure

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Incompletely reverse-transcribed human immunodeficiency virus type 1 genomes in quiescent cells can function as intermediates in the retroviral life cycle

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Reduction in levels of the cyclin-dependent kinase inhibitor p27(kip-1) coupled with transforming growth factor beta neutralization induces cell-cycle entry and increases retroviral transduction of primitive human hematopoietic cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Hematopoietic stem cell quiescence maintained by p21cip1/waf1

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Ex vivo targeting of p21Cip1/Waf1 permits relative expansion of human hematopoietic stem cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Silencing p21(Waf1/Cip1/Sdi1) expression increases gene transduction efficiency in primitive human hematopoietic cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

The fluctuating phenotype of the lymphohematopoietic stem cell with cell cycle transit

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Impaired bone marrow homing of cytokine-activated CD34+ cells in the NOD/SCID model.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Effect of chronic cytokine therapy on clonal dynamics in nonhuman primates

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Hematopoietic stem cell gene therapy: dead or alive?

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Steel factor influences the distribution and activity of murine hematopoietic stem cells in vivo

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Improved retroviral gene transfer into murine and Rhesus peripheral blood or bone marrow repopulating cells primed in vivo with stem cell factor and granulocyte colony-stimulating factor

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Retroviral transduction efficiency of G-CSF+SCF-mobilized peripheral blood CD34+ cells is superior to G-CSF or G-CSF+Flt3-L-mobilized cells in nonhuman primates.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Innovative strategies for PBPC mobilization

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Structure-function based design of small molecule inhibitors targeting Rho family GTPases

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Lentivector-mediated clonal tracking reveals intrinsic heterogeneity in the human hematopoietic stem cell compartment and culture-induced stem cell impairment

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Cytokines: value-added products in hematopoietic stem cell gene therapy

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Efficient lentiviral gene transfer to canine repopulating cells using an overnight transduction protocol

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Efficient gene transfer into rhesus repopulating hematopoietic stem cells using a simian immunodeficiency virus-based lentiviral vector system

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Distinct genomic integration of MLV and SIV vectors in primate hematopoietic stem and progenitor cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Efficiency of transduction of highly purified murine hematopoietic stem cells by lentiviral and oncoretroviral vectors under conditions of minimal in vitro manipulation.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Functional assessment of the engraftment potential of gammaretrovirus-modified CD34+ cells, using a short serum-free transduction protocol

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Highly efficient lentiviral gene transfer in CD34+ and CD34+/38-/lin- cells from mobilized peripheral blood after cytokine prestimulation

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Cytokines, including stem cell factor alone, enhance lentiviral transduction in nondividing human LTCIC and NOD/SCID repopulating cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Factors influencing the titer and infectivity of lentiviral vectors.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Advances in lentiviral vector design for gene-modification of hematopoietic stem cells.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Proteasome activity restricts lentiviral gene transfer into hematopoietic stem cells and is down-regulated by cytokines that enhance transduction.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Stimulation of mouse bone marrow cells with kit ligand, FLT3 ligand, and thrombopoietin leads to efficient retrovirus-mediated gene transfer to stem cells, whereas interleukin 3 and interleukin 11 reduce transduction of short- and long-term repopula

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Converging pathways in leukemogenesis and stem cell self-renewal

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Novel lentiviral vectors displaying "early-acting cytokines" selectively promote survival and transduction of NOD/SCID repopulating human hematopoietic stem cells.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Antiviral activity of the proteasome on incoming human immunodeficiency virus type 1.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Human immunodeficiency virus cDNA metabolism: notable stability of two-long terminal repeat circles

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Retrovirus restriction factors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Intrinsic immunity: a front-line defense against viral attack

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Dependence of human stem cell engraftment and repopulation of NOD/SCID mice on CXCR4

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Modulation of hematopoietic stem cell homing and engraftment by CD26

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Overexpression of CXCR4 on human CD34+ progenitors increases their proliferation, migration, and NOD/SCID repopulation

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Inhibition of CD26 peptidase activity significantly improves engraftment of retrovirally transduced hematopoietic progenitors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Critical factors influencing stable transduction of human CD34(+) cells with HIV-1-derived lentiviral vectors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Fibronectin fragment CH-296 inhibits apoptosis and enhances ex vivo gene transfer by murine retrovirus and human lentivirus vectors independent of viral tropism in nonhuman primate CD34+ cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

The presence of the carboxy-terminal fragment of fibronectin allows maintenance of non-human primate long-term hematopoietic repopulating cells during extended ex vivo culture and transduction.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Busulfan pharmacokinetics, toxicity, and low-dose conditioning for autologous transplantation of genetically modified hematopoietic stem cells in the rhesus macaque model

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Effects of busulfan dose escalation on engraftment of infant rhesus monkey hematopoietic stem cells after gene marking by a lentiviral vector

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Transcription start regions in the human genome are favored targets for MLV integration

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Retroviral DNA integration: ASLV, HIV, and MLV show distinct target site preferences

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Retrovirus vectors: toward the plentivirus?

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

RNA 3' readthrough of oncoretrovirus and lentivirus: implications for vector safety and efficacy

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Retroviral activation of a novel gene encoding a zinc finger protein in IL-3-dependent myeloid leukemia cell lines

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Hematopoietic stem cell gene transfer in a tumor-prone mouse model uncovers low genotoxicity of lentiviral vector integration

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Insertion of retroviral vectors in NOD/SCID repopulating human peripheral blood progenitor cells occurs preferentially in the vicinity of transcription start regions and in introns

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Occurrence of leukaemia following gene therapy of X-linked SCID.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Promoter trapping reveals significant differences in integration site selection between MLV and HIV vectors in primary hematopoietic cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Genotoxicity of retroviral integration in hematopoietic cells.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Murine leukemia induced by retroviral gene marking

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Recurrent retroviral vector integration at the Mds1/Evi1 locus in nonhuman primate hematopoietic cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Acute myeloid leukemia is associated with retroviral gene transfer to hematopoietic progenitor cells in a rhesus macaque

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

EVI1 and hematopoietic disorders: history and perspectives

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Side effects of retroviral gene transfer into hematopoietic stem cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

New genes involved in cancer identified by retroviral tagging

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Retroviral insertional mutagenesis: past, present and future

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Cell-culture assays reveal the importance of retroviral vector design for insertional genotoxicity

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Retroviral expression in embryonic stem cells and hematopoietic stem cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

eGFP reporter genes silence LCRbeta-globin transgene expression via CpG dinucleotides

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Lentiviral vectors for enhanced gene expression in human hematopoietic cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

High-level transduction and gene expression in hematopoietic repopulating cells using a human immunodeficiency [correction of imunodeficiency] virus type 1-based lentiviral vector containing an internal spleen focus forming virus promoter

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Lentivirus gene transfer in murine hematopoietic progenitor cells is compromised by a delay in proviral integration and results in transduction mosaicism and heterogeneous gene expression in progeny cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Enhanced transgene expression in cord blood CD34(+)-derived hematopoietic cells, including developing T cells and NOD/SCID mouse repopulating cells, following transduction with modified trip lentiviral vectors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Genetic induction of immune tolerance to human clotting factor VIII in a mouse model for hemophilia A

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Sustained phenotypic correction of hemophilia a mice following oncoretroviral-mediated expression of a bioengineered human factor VIII gene in long-term hematopoietic repopulating cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Efficient production of human FVIII in hemophilic mice using lentiviral vectors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Recombinant factor VIII expression in hematopoietic cells following lentiviral transduction.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Sustained transgene expression by human cord blood derived CD34+ cells transduced with simian immunodeficiency virus agmTYO1-based vectors carrying the human coagulation factor VIII gene in NOD/SCID mice

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Permanent partial phenotypic correction and tolerance in a mouse model of hemophilia B by stem cell gene delivery of human factor IX.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Stem cell-derived erythroid cells mediate long-term systemic protein delivery

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Silencing and variegation of gammaretrovirus and lentivirus vectors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Virus infection of murine teratocarcinoma stem cell lines

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Silent infection of murine embryonal carcinoma cells by Moloney murine leukemia virus

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

The cHS4 insulator increases the probability of retroviral expression at random chromosomal integration sites.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Genetic manipulation of primate embryonic and hematopoietic stem cells with simian lentivirus vectors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Mutation of CpGs in the murine stem cell virus retroviral vector long terminal repeat represses silencing in embryonic stem cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Retrovirus silencing, variegation, extinction, and memory are controlled by a dynamic interplay of multiple epigenetic modifications

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Independent mechanisms involved in suppression of the Moloney leukemia virus genome during differentiation of murine teratocarcinoma cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Transgenesis by lentiviral vectors: lack of gene silencing in mammalian embryonic stem cells and preimplantation embryos

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Germline transmission and tissue-specific expression of transgenes delivered by lentiviral vectors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Generation of transgenic mice using lentiviral vectors: a novel preclinical assessment of lentiviral vectors for gene therapy

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Retrovirus vector silencing is de novo methylase independent and marked by a repressive histone code

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Development of gene therapy for hematopoietic stem cells using lentiviral vectors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Lentivirus vector gene expression during ES cell-derived hematopoietic development in vitro

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Equal potency of gammaretroviral and lentiviral SIN vectors for expression of O6-methylguanine-DNA methyltransferase in hematopoietic cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

A third-generation lentivirus vector with a conditional packaging system

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Effects of retroviral vector design on expression of human adenosine deaminase in murine bone marrow transplant recipients engrafted with genetically modified cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Hepatitis B virus RNA element that facilitates accumulation of surface gene transcripts in the cytoplasm.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Woodchuck hepatitis virus contains a tripartite posttranscriptional regulatory element.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Woodchuck hepatitis virus posttranscriptional regulatory element enhances expression of transgenes delivered by retroviral vectors.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Context Dependence of Different Modules for Posttranscriptional Enhancement of Gene Expression from Retroviral Vectors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Potential oncogene activity of the woodchuck hepatitis post-transcriptional regulatory element (WPRE).

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Woodchuck hepatitis virus post-transcriptional regulatory element deleted from X protein and promoter sequences enhances retroviral vector titer and expression

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Stem cell gene therapy for the beta-chain hemoglobinopathies. Problems and progress

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Gene therapy progress and prospects: development of improved lentiviral and retroviral vectors--design, biosafety, and production.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Insulators: many functions, many mechanisms.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Position-effect protection and enhancer blocking by the chicken beta-globin insulator are separable activities

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Recruitment of histone modifications by USF proteins at a vertebrate barrier element

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

A chromatin insulator protects retrovirus vectors from chromosomal position effects

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Topological constraints governing the use of the chicken HS4 chromatin insulator in oncoretrovirus vectors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Performance- and safety-enhanced lentiviral vectors containing the human interferon-beta scaffold attachment region and the chicken beta-globin insulator

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Biological significance of unwinding capability of nuclear matrix-associating DNAs

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Human matrix attachment regions insulate transgene expression from chromosomal position effects in Drosophila melanogaster

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Scaffold attachment region-containing retrovirus vectors improve long-term proviral expression after transplantation of GFP-modified CD34+ baboon repopulating cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Hematopoietic stem cell gene therapy with drug resistance genes: an update

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Survival of the fittest: in vivo selection and stem cell gene therapy

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Gene therapy with drug resistance genes

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Protection and in vivo selection of hematopoietic stem cells using temozolomide, O6-benzylguanine, and an alkyltransferase-expressing retroviral vector

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Hematoprotection and enrichment of transduced cells in vivo after gene transfer of MGMT(P140K) into hematopoietic stem cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Successful treatment of murine beta-thalassemia using in vivo selection of genetically modified, drug-resistant hematopoietic stem cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Methylguanine methyltransferase-mediated in vivo selection and chemoprotection of allogeneic stem cells in a large-animal model

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

In vivo selection of MGMT(P140K) lentivirus–transduced human NOD/SCID repopulating cells without pretransplant irradiation conditioning

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Repopulating defect of mismatch repair–deficient hematopoietic stem cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Locus control regions: coming of age at a decade plus

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Locus control regions

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

ChIPs of the beta-globin locus: unraveling gene regulation within an active domain

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Locus control regions of mammalian beta-globin gene clusters: combining phylogenetic analyses and experimental results to gain functional insights

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Position-independent, high-level expression of the human beta-globin gene in transgenic mice

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

The beta-globin dominant control region activates homologous and heterologous promoters in a tissue-specific manner

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Successful treatment of murine beta-thalassemia intermedia by transfer of the human beta-globin gene

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Correction of sickle cell disease in transgenic mouse models by gene therapy

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Permanent and panerythroid correction of murine beta thalassemia by multiple lentiviral integration in hematopoietic stem cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

The degree of phenotypic correction of murine beta -thalassemia intermedia following lentiviral-mediated transfer of a human gamma-globin gene is influenced by chromosomal position effects and vector copy number

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

A novel murine model of Cooley anemia and its rescue by lentiviral-mediated human beta-globin gene transfer

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Correction of a mouse model of sickle cell disease: lentiviral/antisickling beta-globin gene transduction of unmobilized, purified hematopoietic stem cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Extended beta-globin locus control region elements promote consistent therapeutic expression of a gamma-globin lentiviral vector in murine beta-thalassemia

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Successful correction of the human beta-thalassemia major phenotype using a lentiviral vector

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Locus control region of the human CD2 gene in a lentivirus vector confers position-independent transgene expression

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Specific transgene expression in human and mouse CD4+ cells using lentiviral vectors with regulatory sequences from the CD4 gene

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Gene therapy of apolipoprotein E-deficient mice using a novel macrophage-specific retroviral vector

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Targeting transgene expression to antigen-presenting cells derived from lentivirus-transduced engrafting human hematopoietic stem/progenitor cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Trans-splicing repair of CD40 ligand deficiency results in naturally regulated correction of a mouse model of hyper-IgM X-linked immunodeficiency.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

RNA-triggered gene silencing

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Duplexes of 21-nucleotide RNAs mediate RNA interference in cultured mammalian cells

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

RNA interference in adult mice.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Therapeutic applications of RNA interference: recent advances in siRNA design

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Gene therapy progress and prospects: recent progress in transgene and RNAi expression cassettes

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Activation of the interferon system by short-interfering RNAs

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Determinants of interferon-stimulated gene induction by RNAi vectors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Analysis of double-stranded RNA-induced apoptosis pathways using interferon-response noninducible small interfering RNA expression vector library

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

A genetic strategy to treat sickle cell anemia by coregulating globin transgene expression and RNA interference

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Gene transfer in humans using a conditionally replicating lentiviral vector

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

No soluble common cytokine receptor gamma chain (gamma(c)) in activated human lymphocyte cultures-comparison with soluble IL-2Ralpha

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Biochemical and Functional Abnormalities in Lymphocytes from an Adenosine Deaminase-deficient Patient during Enzyme Replacement Therapy

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Immune reconstitution in ADA-SCID after PBL gene therapy and discontinuation of enzyme replacement

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Direct interaction of the Wiskott-Aldrich syndrome protein with the GTPase Cdc42

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Efficacy of gene therapy for Wiskott-Aldrich syndrome using a WAS promoter/cDNA-containing lentiviral vector and nonlethal irradiation.

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021

Correction of murine hemophilia A by hematopoietic stem cell gene therapy

1 reference

https://api.crossref.org/works/10.1038%2FSJ.MT.6300060

7 January 2021