(Q36342335)

13 August 2017

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title

Allele-specific RNA interference for neurological disease (English)

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13 August 2017

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Rodriguez-Lebron E

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13 August 2017

Paulson HL

series ordinal

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13 August 2017

publication date

1 March 2006

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13 August 2017

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13 August 2017

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13 August 2017

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13 August 2017

page(s)

576-581

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RNAi suppresses polyglutamine-induced neurodegeneration in a model of spinocerebellar ataxia.

13 August 2017

cites work

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Intrastriatal rAAV-mediated delivery of anti-huntingtin shRNAs induces partial reversal of disease progression in R6/1 Huntington's disease transgenic mice

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

RNA interference improves motor and neuropathological abnormalities in a Huntington's disease mouse model

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Lentiviral-mediated silencing of SOD1 through RNA interference retards disease onset and progression in a mouse model of ALS.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Silencing mutant SOD1 using RNAi protects against neurodegeneration and extends survival in an ALS model

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Functional siRNAs and miRNAs Exhibit Strand Bias

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Asymmetry in the assembly of the RNAi enzyme complex

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Argonaute2 is the catalytic engine of mammalian RNAi

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Potent and specific genetic interference by double-stranded RNA in Caenorhabditis elegans

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

MicroRNAs: critical regulators of development, cellular physiology and malignancy

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Characterization of Dicer-deficient murine embryonic stem cells.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Processing of primary microRNAs by the Microprocessor complex

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

MicroRNAs: genomics, biogenesis, mechanism, and function

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Functional anatomy of siRNAs for mediating efficient RNAi in Drosophila melanogaster embryo lysate

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Kinetic analysis of the RNAi enzyme complex

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Selective silencing by RNAi of a dominant allele that causes amyotrophic lateral sclerosis

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Targeting Alzheimer's disease genes with RNA interference: an efficient strategy for silencing mutant alleles

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Allele-specific silencing of dominant disease genes

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Ancestral origins of the Machado-Joseph disease mutation: a worldwide haplotype study

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Wild-type huntingtin plays a role in brain development and neuronal survival

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Ancestral differences in the distribution of the delta 2642 glutamic acid polymorphism is associated with varying CAG repeat lengths on normal chromosomes: insights into the genetic evolution of Huntington disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

The early-onset torsion dystonia gene (DYT1) encodes an ATP-binding protein

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

TorsinA: movement at many levels

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Aberrant cellular behavior of mutant torsinA implicates nuclear envelope dysfunction in DYT1 dystonia.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Neuronal proteins custom designed by alternative splicing

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Crystal structure of a PIWI protein suggests mechanisms for siRNA recognition and slicer activity

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Crystal structure of Argonaute and its implications for RISC slicer activity

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

A protein sensor for siRNA asymmetry

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Structural insights into mRNA recognition from a PIWI domain-siRNA guide complex

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Structural basis for 5'-end-specific recognition of guide RNA by the A. fulgidus Piwi protein

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

The contributions of dsRNA structure to Dicer specificity and efficiency

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

U6 promoter-driven siRNAs with four uridine 3' overhangs efficiently suppress targeted gene expression in mammalian cells.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Transcription and processing of human microRNA precursors

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Efficient processing of primary microRNA hairpins by Drosha requires flanking nonstructured RNA sequences

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Use of RNA polymerase II to transcribe artificial microRNAs.

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Potent and persistent in vivo anti-HBV activity of chemically modified siRNAs

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

RNA interference and chemically modified small interfering RNAs

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Small non-coding RNAs as magic bullets

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Therapeutic silencing of an endogenous gene by systemic administration of modified siRNAs

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

Toward therapy for DYT1 dystonia: allele-specific silencing of mutant TorsinA

21 January 2018

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

inferred from DOI database lookup

7 January 2021

based on heuristic

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

inferred from DOI database lookup

7 January 2021

based on heuristic

Antibody mediated in vivo delivery of small interfering RNAs via cell-surface receptors

1 reference

https://api.crossref.org/works/10.1038%2FSJ.GT.3302702

inferred from DOI database lookup

7 January 2021

based on heuristic

Identifiers

DOI

10.1038/SJ.GT.3302702

1 reference

Dimensions Publication ID

13 August 2017

1005935261

0 references

1 reference