(Q33389419)
Statements
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A phase 2 study of eliglustat tartrate (Genz-112638), an oral substrate reduction therapy for Gaucher disease type 1. (English)
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Gregory M Pastores
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Elena Lukina
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Nora Watman
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Elsa Avila Arreguin
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Maryam Banikazemi
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Marta Dragosky
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Marcelo Iastrebner
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Hanna Rosenbaum
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Mici Phillips
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Daniel I Rosenthal
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Mathilde Kaper
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Tejdip Singh
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Ana Cristina Puga
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Peter L Bonate
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M Judith Peterschmitt
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3 May 2010
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116
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893-899
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Identifiers
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