(Q59069004)

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Elizabeth A. Buzney

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Mohamed K. Khan

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Alan F. Flint

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Louis M. Kunkel

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Richard C. Mulligan

The basic science of gene therapy

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language of work or name

English

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publication date

September 1999

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published in

Nature

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volume

401

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issue

6751

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page(s)

390-394

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cites work

1 reference

7 January 2021

The molecular basis of muscular dystrophy in the mdx mouse: a point mutation

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7 January 2021

Nuclear domains in muscle cells

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7 January 2021

Localization of muscle gene products in nuclear domains

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7 January 2021

The fate of individual myoblasts after transplantation into muscles of DMD patients

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7 January 2021

Somatic reversion/suppression of the mouse mdx phenotype in vivo.

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7 January 2021

Muscle regeneration by bone marrow-derived myogenic progenitors

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7 January 2021

Recruitment of bone-marrow-derived cells by skeletal and cardiac muscle in adult dystrophic mdx mice

1 reference

7 January 2021

Isolation and functional properties of murine hematopoietic stem cells that are replicating in vivo

1 reference

7 January 2021

Dye efflux studies suggest that hematopoietic stem cells expressing low or undetectable levels of CD34 antigen exist in multiple species.

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7 January 2021

Primary mouse myoblast purification, characterization, and transplantation for cell-mediated gene therapy

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7 January 2021

Satellite cell of skeletal muscle fibers

1 reference

7 January 2021

Conversion of mdx myofibres from dystrophin-negative to -positive by injection of normal myoblasts

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7 January 2021

Invited review: myoblast transfer: a possible therapy for inherited myopathies?

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7 January 2021

Human dystrophin expression in mdx mice after intramuscular injection of DNA constructs

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7 January 2021

Efficient adenovirus-mediated transfer of a human minidystrophin gene to skeletal muscle of mdx mice

1 reference

7 January 2021

A new adenoviral vector: Replacement of all viral coding sequences with 28 kb of DNA independently expressing both full-length dystrophin and beta-galactosidase

1 reference

7 January 2021

Prevention of dystrophic pathology in mdx mice by a truncated dystrophin isoform.

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7 January 2021

Expression of full-length and truncated dystrophin mini-genes in transgenic mdx mice

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7 January 2021

Cultured adherent cells from marrow can serve as long-lasting precursor cells for bone, cartilage, and lung in irradiated mice

1 reference

7 January 2021

Myogenic Expression of Mesenchymal Stem Cells within Myotubes of mdx Mice in Vitro and in Vivo

1 reference

7 January 2021

Marrow stromal cells as stem cells for nonhematopoietic tissues

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7 January 2021

Isolation of putative progenitor endothelial cells for angiogenesis

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7 January 2021

Turning brain into blood: a hematopoietic fate adopted by adult neural stem cells in vivo

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7 January 2021

Heterogeneity in the progeny of single human muscle satellite cells

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7 January 2021

Rapid detection of human chromosome 21 aberrations by in situ hybridization

1 reference

7 January 2021

A method to codetect introduced genes and their products in gene therapy protocols

1 reference

7 January 2021