Pages that link to "Q36728106"
The following pages link to Trans-splicing adeno-associated viral vector-mediated gene therapy is limited by the accumulation of spliced mRNA but not by dual vector coinfection efficiency (Q36728106):
Displaying 25 items.
- A hybrid vector system expands adeno-associated viral vector packaging capacity in a transgene-independent manner (Q28256353) (← links)
- AAV recombineering with single strand oligonucleotides (Q33514824) (← links)
- Partial restoration of cardiac function with ΔPDZ nNOS in aged mdx model of Duchenne cardiomyopathy (Q33649295) (← links)
- Evidence for the failure of adeno-associated virus serotype 5 to package a viral genome > or = 8.2 kb. (Q33730469) (← links)
- Full-length dystrophin reconstitution with adeno-associated viral vectors (Q33782799) (← links)
- Adeno-associated virus serotype-9 microdystrophin gene therapy ameliorates electrocardiographic abnormalities in mdx mice. (Q33925312) (← links)
- Gene therapy progress and prospects: Duchenne muscular dystrophy (Q34576814) (← links)
- Whole body skeletal muscle transduction in neonatal dogs with AAV-9. (Q35053768) (← links)
- SERCA2a gene transfer improves electrocardiographic performance in aged mdx mice (Q35183186) (← links)
- Gene therapy progress and prospects--vectorology: design and production of expression cassettes in AAV vectors (Q36384464) (← links)
- Treatment of human disease by adeno-associated viral gene transfer (Q36448393) (← links)
- Synthetic intron improves transduction efficiency of trans-splicing adeno-associated viral vectors. (Q36728109) (← links)
- Efficient whole-body transduction with trans-splicing adeno-associated viral vectors (Q36968872) (← links)
- Efficient in vivo gene expression by trans-splicing adeno-associated viral vectors (Q36968876) (← links)
- Expanding adeno-associated viral vector capacity: a tale of two vectors. (Q37024689) (← links)
- Oversized AAV transductifon is mediated via a DNA-PKcs-independent, Rad51C-dependent repair pathway (Q37393799) (← links)
- Translational research and therapeutic perspectives in dysferlinopathies. (Q37873747) (← links)
- Arginine-based cationic liposomes for efficient in vitro plasmid DNA delivery with low cytotoxicity (Q39847510) (← links)
- Correction of DNA protein kinase deficiency by spliceosome-mediated RNA trans-splicing and sleeping beauty transposon delivery (Q40141498) (← links)
- A comparison of AAV strategies distinguishes overlapping vectors for efficient systemic delivery of the 6.2 kb Dysferlin coding sequence (Q40884119) (← links)
- Delivering Transgenic DNA Exceeding the Carrying Capacity of AAV Vectors (Q41093443) (← links)
- Cochlear Gene Therapy for Sensorineural Hearing Loss: Current Status and Major Remaining Hurdles for Translational Success. (Q55657184) (← links)
- Ex Vivo/In vivo Gene Editing in Hepatocytes Using "All-in-One" CRISPR-Adeno-Associated Virus Vectors with a Self-Linearizing Repair Template (Q92324014) (← links)
- Cytosine and adenine base editing of the brain, liver, retina, heart and skeletal muscle of mice via adeno-associated viruses (Q92643998) (← links)
- Adeno-Associated Viral Vectors as a Tool for Large Gene Delivery to the Retina (Q93005504) (← links)