Pages that link to "Q35678425"
The following pages link to Novel mini-dystrophin gene dual adeno-associated virus vectors restore neuronal nitric oxide synthase expression at the sarcolemma (Q35678425):
Displaying 50 items.
- Promising and delivering gene therapies for vision loss (Q27007079) (← links)
- Gene therapy of inherited retinal degenerations: prospects and challenges (Q27009261) (← links)
- Animal models of Duchenne muscular dystrophy: from basic mechanisms to gene therapy (Q28084979) (← links)
- Taking down the FLAG! How insect cell expression challenges an established tag-system (Q28728764) (← links)
- The Dystrophin Complex: Structure, Function, and Implications for Therapy (Q30376293) (← links)
- Gene transfer in skeletal and cardiac muscle using recombinant adeno-associated virus (Q30539495) (← links)
- Lentiviral vectors can be used for full-length dystrophin gene therapy (Q33668822) (← links)
- Therapy of Genetic Disorders-Novel Therapies for Duchenne Muscular Dystrophy (Q33678893) (← links)
- Genome Editing and Muscle Stem Cells as a Therapeutic Tool for Muscular Dystrophies (Q33729585) (← links)
- Full-length dystrophin reconstitution with adeno-associated viral vectors (Q33782799) (← links)
- The potential of adeno-associated viral vectors for gene delivery to muscle tissue (Q33902499) (← links)
- Spell Checking Nature: Versatility of CRISPR/Cas9 for Developing Treatments for Inherited Disorders (Q34045672) (← links)
- Novel adeno-associated viruses derived from pig tissues transduce most major organs in mice (Q34384998) (← links)
- Phosphorylation within the cysteine-rich region of dystrophin enhances its association with β-dystroglycan and identifies a potential novel therapeutic target for skeletal muscle wasting (Q34575694) (← links)
- Natural history of cone disease in the murine model of Leber congenital amaurosis due to CEP290 mutation: determining the timing and expectation of therapy (Q35132187) (← links)
- Duchenne muscular dystrophy gene therapy in the canine model. (Q35641673) (← links)
- Immobilization of FLAG-Tagged Recombinant Adeno-Associated Virus 2 onto Tissue Engineering Scaffolds for the Improvement of Transgene Delivery in Cell Transplants (Q35649962) (← links)
- Porcine models of muscular dystrophy (Q35974809) (← links)
- In vivo gene transfer strategies to achieve partial correction of von Willebrand disease. (Q36084450) (← links)
- Autologous skeletal muscle derived cells expressing a novel functional dystrophin provide a potential therapy for Duchenne Muscular Dystrophy (Q36506919) (← links)
- Expressing Transgenes That Exceed the Packaging Capacity of Adeno-Associated Virus Capsids (Q36601946) (← links)
- Progress in gene therapy of dystrophic heart disease (Q36773242) (← links)
- Retinal gene therapy with a large MYO7A cDNA using adeno-associated virus (Q36808032) (← links)
- Prospect of gene therapy for cardiomyopathy in hereditary muscular dystrophy (Q37021623) (← links)
- Dual AAV therapy ameliorates exercise-induced muscle injury and functional ischemia in murine models of Duchenne muscular dystrophy (Q37111962) (← links)
- Genomic removal of a therapeutic mini-dystrophin gene from adult mice elicits a Duchenne muscular dystrophy-like phenotype (Q37530255) (← links)
- Dual adeno-associated virus vectors result in efficient in vitro and in vivo expression of an oversized gene, MYO7A. (Q37710671) (← links)
- Update on the treatment of Duchenne muscular dystrophy (Q38074834) (← links)
- Repair or replace? Exploiting novel gene and cell therapy strategies for muscular dystrophies (Q38079633) (← links)
- New developments in the use of gene therapy to treat Duchenne muscular dystrophy (Q38168863) (← links)
- Concise review: mesoangioblast and mesenchymal stem cell therapy for muscular dystrophy: progress, challenges, and future directions (Q38267714) (← links)
- Dual AAV gene therapy for Duchenne muscular dystrophy with a 7-kb mini-dystrophin gene in the canine model (Q38631895) (← links)
- Copackaging of multiple adeno-associated viral vectors in a single production step (Q38964154) (← links)
- A Hypothesis for Examining Skeletal Muscle Biopsy-Derived Sarcolemmal nNOSμ as Surrogate for Enteric nNOSα Function (Q38973194) (← links)
- Nanotherapy for Duchenne muscular dystrophy (Q39233936) (← links)
- Therapeutic strategies to address neuronal nitric oxide synthase deficiency and the loss of nitric oxide bioavailability in Duchenne Muscular Dystrophy. (Q39330717) (← links)
- A comparison of AAV strategies distinguishes overlapping vectors for efficient systemic delivery of the 6.2 kb Dysferlin coding sequence (Q40884119) (← links)
- Delivering Transgenic DNA Exceeding the Carrying Capacity of AAV Vectors (Q41093443) (← links)
- A Five-Repeat Micro-Dystrophin Gene Ameliorated Dystrophic Phenotype in the Severe DBA/2J-mdx Model of Duchenne Muscular Dystrophy (Q41171772) (← links)
- Systemic delivery of tyrosine-mutant AAV vectors results in robust transduction of neurons in adult mice (Q41471833) (← links)
- Post-natal induction of PGC-1α protects against severe muscle dystrophy independently of utrophin. (Q41911490) (← links)
- Genome engineering: a new approach to gene therapy for neuromuscular disorders. (Q41928233) (← links)
- Duchenne muscular dystrophy gene therapy in the canine model (Q42175045) (← links)
- An E3-14.7K peptide that promotes microtubules-mediated transport of plasmid DNA increases polyplexes transfection efficiency (Q45887462) (← links)
- Enhancing Endogenous Nitric Oxide by Whole Body Periodic Acceleration Elicits Neuroprotective Effects in Dystrophic Neurons. (Q52723891) (← links)
- Adeno-associated Virus (AAV) Dual Vector Strategies for Gene Therapy Encoding Large Transgenes. (Q52743732) (← links)
- Lentiviral vectors can be used for full-length dystrophin gene therapy. (Q53426367) (← links)
- Humanizing the mdx mouse model of DMD: the long and the short of it. (Q55010648) (← links)
- Systemic AAV Micro-dystrophin Gene Therapy for Duchenne Muscular Dystrophy (Q57039821) (← links)
- Dystrophin R16/17-syntrophin PDZ fusion protein restores sarcolemmal nNOSμ (Q59333111) (← links)