Alternative therapies to address the unmet medical needs of patients with phenylketonuria. (Q54273999)

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English	Alternative therapies to address the unmet medical needs of patients with phenylketonuria.	scientific article

Statements

instance of

scholarly article

1 reference

stated in

Europe PubMed Central

PubMed publication ID

25660215

retrieved

27 May 2018

reference URL

http://europepmc.org/abstract/MED/25660215

editorial

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title

Alternative therapies to address the unmet medical needs of patients with phenylketonuria. (English)

1 reference

stated in

Europe PubMed Central

PubMed publication ID

25660215

retrieved

27 May 2018

reference URL

http://europepmc.org/abstract/MED/25660215

main subject

phenylketonuria

1 reference

based on heuristic

inferred from title

author

Nenad Blau

series ordinal

1

1 reference

stated in

Europe PubMed Central

PubMed publication ID

25660215

retrieved

27 May 2018

reference URL

http://europepmc.org/abstract/MED/25660215

Nicola Longo

series ordinal

2

1 reference

stated in

Europe PubMed Central

PubMed publication ID

25660215

retrieved

27 May 2018

reference URL

http://europepmc.org/abstract/MED/25660215

language of work or name

English

0 references

publication date

7 February 2015

1 reference

stated in

Europe PubMed Central

PubMed publication ID

25660215

retrieved

27 May 2018

reference URL

http://europepmc.org/abstract/MED/25660215

published in

Expert Opinion on Pharmacotherapy

1 reference

stated in

Europe PubMed Central

PubMed publication ID

25660215

retrieved

27 May 2018

reference URL

http://europepmc.org/abstract/MED/25660215

volume

16

1 reference

stated in

Europe PubMed Central

PubMed publication ID

25660215

retrieved

27 May 2018

reference URL

http://europepmc.org/abstract/MED/25660215

issue

6

1 reference

stated in

Europe PubMed Central

PubMed publication ID

25660215

retrieved

27 May 2018

reference URL

http://europepmc.org/abstract/MED/25660215

page(s)

791-800

1 reference

stated in

Europe PubMed Central

PubMed publication ID

25660215

retrieved

27 May 2018

reference URL

http://europepmc.org/abstract/MED/25660215

cites work

The PAH gene, phenylketonuria, and a paradigm shift

1 reference

stated in

Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Challenges and pitfalls in the management of phenylketonuria

1 reference

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Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Large neutral amino acids in the treatment of PKU: from theory to practice

1 reference

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Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Novel pharmacological chaperones that correct phenylketonuria in mice.

1 reference

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Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Tetrahydrobiopterin, its mode of action on phenylalanine hydroxylase, and importance of genotypes for pharmacological therapy of phenylketonuria.

1 reference

stated in

Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Molecular genetics and diagnosis of phenylketonuria: state of the art.

1 reference

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Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Predicted effects of missense mutations on native-state stability account for phenotypic outcome in phenylketonuria, a paradigm of misfolding diseases

1 reference

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Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Effects of sapropterin on endothelium-dependent vasodilation in patients with CADASIL: a randomized controlled trial

1 reference

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Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Preclinical evaluation of multiple species of PEGylated recombinant phenylalanine ammonia lyase for the treatment of phenylketonuria

1 reference

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Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Evaluation of orally administered PEGylated phenylalanine ammonia lyase in mice for the treatment of Phenylketonuria

1 reference

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Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Single-dose, subcutaneous recombinant phenylalanine ammonia lyase conjugated with polyethylene glycol in adult patients with phenylketonuria: an open-label, multicentre, phase 1 dose-escalation trial

1 reference

stated in

Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Erythrocytes encapsulated with phenylalanine hydroxylase exhibit improved pharmacokinetics and lowered plasma phenylalanine levels in normal mice

1 reference

stated in

Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Erythrocyte-mediated delivery of phenylalanine ammonia lyase for the treatment of phenylketonuria in BTBR-Pah(enu2) mice.

1 reference

stated in

Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Efficacy of sapropterin dihydrochloride (tetrahydrobiopterin, 6R-BH4) for reduction of phenylalanine concentration in patients with phenylketonuria: a phase III randomised placebo-controlled study

1 reference

stated in

Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

The response of patients with phenylketonuria and elevated serum phenylalanine to treatment with oral sapropterin dihydrochloride (6R-tetrahydrobiopterin): a phase II, multicentre, open-label, screening study

1 reference

stated in

Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Efficacy of sapropterin dihydrochloride in increasing phenylalanine tolerance in children with phenylketonuria: a phase III, randomized, double-blind, placebo-controlled study

1 reference

stated in

Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Longitudinal quality of life analysis in a phenylketonuria cohort provided sapropterin dihydrochloride

1 reference

stated in

Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Sapropterin dihydrochloride use in pregnant women with phenylketonuria: an interim report of the PKU MOMS sub-registry

1 reference

stated in

Crossref

reference URL

https://api.crossref.org/works/10.1517%2F14656566.2015.1013030

retrieved

21 January 2018

Identifiers

DOI

10.1517/14656566.2015.1013030

1 reference

stated in

Europe PubMed Central

PubMed publication ID

25660215

retrieved

27 May 2018

reference URL

http://europepmc.org/abstract/MED/25660215

PubMed publication ID

25660215

1 reference

stated in

Europe PubMed Central

PubMed publication ID

25660215

retrieved

27 May 2018

reference URL

http://europepmc.org/abstract/MED/25660215

ResearchGate publication ID

272099911

0 references

 

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