Nanopolymers improve delivery of exon skipping oligonucleotides and concomitant dystrophin expression in skeletal muscle of mdx mice (Q33326762)

25 July 2017

title

Nanopolymers improve delivery of exon skipping oligonucleotides and concomitant dystrophin expression in skeletal muscle of mdx mice (English)

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25 July 2017

Jason H Williams

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25 July 2017

Rebecca C Schray

series ordinal

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25 July 2017

Shashank R Sirsi

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25 July 2017

Gordon J Lutz

series ordinal

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25 July 2017

language of work or name

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2 April 2008

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25 July 2017

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25 July 2017

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25 July 2017

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describes a project that uses

25 July 2017

ImageJ

1 reference

11 June 2022

https://www.ebi.ac.uk/europepmc/webservices/rest/PMC2362111/fullTextXML

inferred from PubMed Central ID database lookup

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21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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31 October 2018

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Poly(ethylene imine)-poly(ethylene glycol) copolymers facilitate efficient delivery of antisense oligonucleotides to nuclei of mature muscle cells of mdx mice

31 October 2018

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31 October 2018

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31 October 2018

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31 October 2018

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Alternative splicing in disease and therapy

31 October 2018

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31 October 2018

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Morpholino antisense oligonucleotide induced dystrophin exon 23 skipping in mdx mouse muscle.

31 October 2018

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Functional amounts of dystrophin produced by skipping the mutated exon in the mdx dystrophic mouse

31 October 2018

1 reference

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Therapeutic antisense-induced exon skipping in cultured muscle cells from six different DMD patients.

31 October 2018

1 reference

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Microbubble ultrasound improves the efficiency of gene transduction in skeletal muscle in vivo with reduced tissue damage

31 October 2018

1 reference

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Relocalization of neuronal nitric oxide synthase (nNOS) as a marker for complete restoration of the dystrophin associated protein complex in skeletal muscle

31 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2362111

Targeted exon skipping as a potential gene correction therapy for Duchenne muscular dystrophy.

31 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2362111

Polyion complex micelles with protein-modified corona for receptor-mediated delivery of oligonucleotides into cells.

31 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2362111

Expression of full-length and truncated dystrophin mini-genes in transgenic mdx mice

31 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2362111

Expression of human full-length and minidystrophin in transgenic mdx mice: implications for gene therapy of Duchenne muscular dystrophy

31 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2362111

Enhanced in vivo delivery of antisense oligonucleotides to restore dystrophin expression in adult mdx mouse muscle

31 October 2018

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12 December 2020

Morpholino oligomer-mediated exon skipping averts the onset of dystrophic pathology in the mdx mouse

1 reference

12 December 2020

PEG-PEI copolymers for oligonucleotide delivery to cells and tissues

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12 December 2020

The structure of PEG-modified poly(ethylene imines) influences biodistribution and pharmacokinetics of their complexes with NF-kappaB decoy in mice

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12 December 2020

Intracellular route and transcriptional competence of polyethylenimine-DNA complexes

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12 December 2020

Improved antisense oligonucleotide induced exon skipping in the mdx mouse model of muscular dystrophy

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12 December 2020

Induction of dystrophin expression by exon skipping in mdx mice following intramuscular injection of antisense oligonucleotides complexed with PEG-PEI copolymers

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12 December 2020

Exploring the frontiers of therapeutic exon skipping for Duchenne muscular dystrophy by double targeting within one or multiple exons

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12 December 2020

Identifiers

DOI

10.1186/1472-6750-8-35

1 reference

Dimensions Publication ID

25 July 2017

0 references

1 reference

25 July 2017

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