Theodore E. Woodward Award. AAV-mediated gene transfer for hemophilia (Q35157358)

6 August 2017

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title

Theodore E. Woodward Award. AAV-mediated gene transfer for hemophilia (English)

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6 August 2017

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Katherine A High

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6 August 2017

publication date

1 January 2003

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Transactions of the American Clinical and Climatological Association

6 August 2017

published in

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6 August 2017

volume

114

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6 August 2017

page(s)

337-51; discussion 351-2

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The Chapel Hill hemophilia A dog colony exhibits a factor VIII gene inversion

6 August 2017

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Gene transfer as an approach to treating hemophilia

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Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector.

13 July 2018

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13 July 2018

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A factor IX-deficient mouse model for hemophilia B gene therapy

13 July 2018

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Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors

13 July 2018

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Haemophilia prophylaxis in young patients--a long-term follow-up

13 July 2018

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Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus

13 July 2018

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Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein

13 July 2018

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A combined management protocol for patients with coagulation disorders infected with hepatitis C virus

13 July 2018

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A deletion mutation causes hemophilia B in Lhasa Apso dogs

13 July 2018

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13 July 2018

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13 July 2018

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In vivo gene therapy of hemophilia B: sustained partial correction in factor IX-deficient dogs

13 July 2018

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Adenovirus-mediated urokinase gene transfer induces liver regeneration and allows for efficient retrovirus transduction of hepatocytes in vivo

13 July 2018

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Production of human factor IX in animals by genetically modified skin fibroblasts: potential therapy for hemophilia B.

13 July 2018

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1986 update of HIV seroprevalence, seroconversion, AIDS incidence, and immunologic correlates of HIV infection in patients with hemophilia A and B.

13 July 2018

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Molecular cloning of a cDNA encoding canine factor IX.

13 July 2018

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Canine hemophilia B resulting from a point mutation with unusual consequences

13 July 2018

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Deduced amino acid sequence of mouse blood-coagulation factor IX.

13 July 2018

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Expression of human factor IX in rat capillary endothelial cells: toward somatic gene therapy for hemophilia B

13 July 2018

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Expression of human factor IX in mice after injection of genetically modified myoblasts

13 July 2018

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The current status of clinical gene therapy

13 July 2018

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Sustained phenotypic correction of hemophilia B dogs with a factor IX null mutation by liver-directed gene therapy

27 September 2018

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Lack of germline transmission of vector sequences following systemic administration of recombinant AAV-2 vector in males

27 September 2018

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Gene therapy in haematology and oncology

27 September 2018

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Posttranslational modifications of recombinant myotube-synthesized human factor IX.

27 September 2018

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Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors

27 September 2018

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Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector

27 September 2018

1 reference

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Targeted inactivation of the coagulation factor IX gene causes hemophilia B in mice.

27 September 2018

1 reference

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Adeno-associated viral vector-mediated gene transfer of human blood coagulation factor IX into mouse liver

27 September 2018

1 reference

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Investigation of chronic hepatitis C infection in individuals with haemophilia: assessment of invasive and non-invasive methods

27 September 2018

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Targeted disruption of the mouse factor VIII gene produces a model of haemophilia A

27 September 2018

1 reference

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The canine factor VIII cDNA and 5' flanking sequence

27 September 2018

1 reference

12 December 2020

A phase I/II study of tgAAV-CF for the treatment of chronic sinusitis in patients with cystic fibrosis

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12 December 2020

Efficient and persistent gene transfer of AAV-CFTR in maxillary sinus

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12 December 2020

FDA comments on phase I clinical trials without vector biodistribution data

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12 December 2020

Trial halted after gene shows up in semen

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12 December 2020

Modern treatment of hemophilia: from the shadows towards the light

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12 December 2020

Intraobserver and interobserver variations in liver biopsy interpretation in patients with chronic hepatitis C. The French METAVIR Cooperative Study Group

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12 December 2020

Identifiers

PMC publication ID

2194524

1 reference

6 August 2017

1 reference